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    • About 
      • Board of Directors 
        • Giovanni Caforio 
        • Simon Moroney 
        • Nancy C. Andrews 
        • Ton Buechner 
        • Patrice Bula 
        • Elizabeth (Liz) Doherty 
        • Ana de Pro Gonzalo 
        • Bridgette Heller 
        • Daniel Hochstrasser 
        • Frans van Houten 
        • Elizabeth McNally 
        • John D. Young 
        • Charlotte Pamer-Wieser 
      • Executive Committee 
        • Vasant (Vas) Narasimhan 
        • Shreeram Aradhye 
        • Victor Bulto 
        • Aharon (Ronny) Gal 
        • Karen L. Hale 
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      About

      Novartis is an innovative medicines company. Every day, we work to reimagine medicine to improve and extend people’s lives so that patients, healthcare professionals and societies are empowered in the face of serious disease. Our medicines reach 296 million people worldwide.

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      Research & development

      Discover how Novartis turns breakthrough science into transformative, high-value treatments.
       

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      Learn about our commitments to making a positive impact on the world by providing access to innovative medicines, protecting the environment, and upholding high ethical standards. Explore the Novartis in Society Integrated Report.

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      Careers

      Novartis is hiring! Find open positions, learn more about our strategy and culture, and apply today.

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    Home

    Working together, we can reimagine medicine to improve and extend people’s lives.

OAV101

onasemnogene abeparvovec
Neuroscience
Registration
2025
Survival motor neuron (SMN1) gene replacement therapy
SMA IT administration
Supplementary Indication
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